- OUR CORPORATE FRIENDS -
Meet our friends who are doing their bit to support our #RareRevolution
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- EVENTS -
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Global Gene’s RARE Patient Advocacy Summit is the world’s largest gathering of rare disease patients, caregivers, thought leaders and stakeholders. This event is an unparalleled opportunity to forge meaningful connections with other rare advocates and take home actionable strategies and tools to accelerate change. Join us for the 2019 RARE Patient Advocacy Summit in San Diego, September 18-20, 2019. |
RAREsummit19 is a 1 day summit focusing on patient-centricity in rare disease progress. What if we were able to share information with the power to revolutionise the current rare disease landscape? What if we could provide solutions to patients now, answering their pressing questions about their disease, care, and treatment? What if we could ensure that patients and advocates played an equal and vital role in the development of drugs, assistive technologies, and healthcare? Rare disease patients and their families are tired of waiting for answers and the slow pace of change. They want to be involved and share their lived experiences to help companies, researchers and healthcare professionals find answers and solutions. Hear from, learn from and engage in cross-sector activities with a range of stakeholders: patients; patient advocacy groups; researchers; health care professionals and companies who are leading the way in pioneering partnerships to accelerate change.
Join the Cambridge Rare Disease Network at the Wellcome Genome Campus: a hub of life-changing science. We think it’s the perfect venue to make progress for rare diseases.
For more information please visit https://camraredisease.org/summit-2019/
SMi Group are proud to announce the 9th Annual Orphan Drugs and Rare Diseases Conference, taking place on the 15th and 16th October 2019 in London, UK.
The orphan drug market is continuously growing and is expected to reach $176 billion by 2020, with a CGR of 10.5% just for orphan drugs – this is twice the growth rate of the overall prescription drug market (5.3% CGR from 2014-2020). By 2020, orphan drugs are set to account for 19% of global prescription sales.
This is due to the arising interest from pharmaceutical companies for underlying benefits, such as the potential discovery of mechanisms for more common diseases, and also the involvement of many smaller biotechnology start-up companies who are primarily focused on rare diseases.
The 2019 agenda features various key presentations by leading solution providers, biotechnology companies, clinical researchers, regulatory professionals and charity leaders discussing possible ways to accelerate orphan drug development and access to rare disease patients, including the introduction of recent technologies and products to help aid the access of orphan drugs.
BENEFITS OF ATTENDING
PLUS AN INTERACTIVE HALF-DAY POST-CONFERENCE WORKSHOP - Thursday 17th October 2019
A deep dive into strategies for accelerating patient access of orphan drugs
Workshop Leaders: Solange Corriol-Rohou, Senior Director Regulatory Affairs & Policy Europe, AstraZeneca
Cecile Ollivier, Chief Operating Officer, Aparito
- HEAR about the success of integrated approaches to develop a robust early access and evidence generation plan with Bionical Emas
- DISCUSS the intervention of pharmaceutical companies and patient advocates in developing lifelong rare disease treatments with Takeda
- EXPLORE the current development of strategies aimed to improve patient access to orphan drugs with Genetic Alliance UK
- GAIN INSIGHT into the various challenges facing orphan drug development with Minoryx Therapeutics
PLUS AN INTERACTIVE HALF-DAY POST-CONFERENCE WORKSHOP - Thursday 17th October 2019
A deep dive into strategies for accelerating patient access of orphan drugs
Workshop Leaders: Solange Corriol-Rohou, Senior Director Regulatory Affairs & Policy Europe, AstraZeneca
Cecile Ollivier, Chief Operating Officer, Aparito
SMi’s 9th Annual Orphan Drugs & Rare Diseases Conference
Conference: Tuesday 15 and Wednesday 16 October 2019
Workshop: Thursday 17th October 2019
Location: Holiday Inn Kesington Forum, London, UK
Website: http://www.orphandrugs.co.uk/rarediseasemagwl
Conference: Tuesday 15 and Wednesday 16 October 2019
Workshop: Thursday 17th October 2019
Location: Holiday Inn Kesington Forum, London, UK
Website: http://www.orphandrugs.co.uk/rarediseasemagwl
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There are over 7,000 rare diseases and 90% of them are still without an approved treatment. Attendees of the largest and longest standing rare disease conference, NORD’s Rare Diseases & Orphan Products Breakthrough Summit will explore why “The Time is Now”—for research, innovation, advocacy and collaboration. The Rare Summit affords an unprecedented opportunity to hear from the experts, including the heads of the three FDA medical centres, and join conversations of the pressing issues facing the rare disease community. From addressing affordability while sustaining innovation and creating a roadmap for collaboration between patient organisations and industry, to interactive conversations with FDA senior staff, the largest multi-stakeholder event in rare diseases focuses on timely issues with the leading subject matter experts. |
Orphan Drugs
12 – 14 November, Hotel SOFIA, Barcelona
Now recognised as the largest and most established European orphan drug event, we are once again proud to deliver another outstanding speaker line-up and a content-filled agenda that represents the whole orphan drug landscape. The 10th annual event will address the strategic and commercial aspects of bringing new treatments to patients who suffer from rare diseases.
For 2019 we will be expanding the meeting further with a dedicated co-conference on Cell & Gene Therapy and even more dedicated content and tracks than ever before on Clinical/Product Development, Market Access & Pricing, Manufacture, Science & Strategy, Pitch & Partner and Precision Medicine. We will also continue the highly popular Pre-Congress Workshops.
BioData World Congress
4th - 5th December, Basel
BioData World is Europe's largest big data in pharmaceutical development and healthcare congress. The congress was initially designed through a partnership with EMBL-EBI and the Sanger Institute four years ago to tackle the issues of driving big data into the clinic and pharmaceutical development in the most streamlined way possible.
The event will showcase innovation, demonstrate success and break through the obstacles and barriers to ensure that the innovations in genomics and big data enter the clinic with speed and efficiency. It will aim to make the dream of stratified medicine a reality.