Close
×
Subscribe Now
By entering these details you are signing up to receive our newsletter.
First Name
Last Name
Your Email
Type of visitor?
Individuals with a rare condition
Caregiver/family member
Industry/biotech/pharma
Healthcare professionals
Charity/advocate
General interest
Newsletters
RAREBite Newsletter Subscribers (Twice Weekly)
Magazine and RARE Round-Up Weekly Newsletter
Latest Edition
Subscribe Now
Home
Meet the team
Magazine
RARE INSIGHTS
A day in the life
Charity & advocacy
Editor’s picks
Industry insights
Medical
News
Patient voice
RARE employment
RARE parenting
RARE ramblings
RARE REV-inar
Science & tech
Sunday sessions
Turning the tide for rare disease
THE PEOPLE OF RARE
Digital Spotlight
RARE Reports
Resources
Charity Partners
WORK WITH US
Rare Revolutionaries
Community Gallery
Rare Youth
Latest Edition
Subscribe Now
To use more accessibility options, please use a different browser such as Chrome or Firefox.
Press releases
Press releases
Launching CamRARE’s ‘The Need for a RARE Patient Passport’ Report for Rare Disease Day
By admin
1 March 2024
Press releases
Coave Therapeutics Receives Grant from the ALS Association to Advance its CTx-TFEB Program as a Potential Treatment for All Forms of ALS
By admin
29 February 2024
Press releases
SMA Europe launches “Care for adults living with SMA in Europe: a benchmarking report.”
By admin
29 February 2024
Press releases
£1.5 million new fund launched to ‘Help the Heart’
By admin
27 February 2024
Press releases
Blueprint Medicines highlights AYVAKIT® (avapritinib) long-term efficacy and safety data and advances in mast cell disease research at 2024 AAAAI annual meeting
By admin
23 February 2024
Press releases
CureDuchenne hosts “Champions in Miami” event on March 9 to help find a cure for Duchenne muscular dystrophy
By admin
23 February 2024
Press releases
CMT Research Foundation partners to advance study of CMT type 1J by Dr Stephan Zuchner
By admin
21 February 2024
Press releases
Patients as Partners in Clinical Research Conference 2024
By admin
19 February 2024
Charity & advocacy
Rare Disease Awareness Day Calendar
By admin
14 February 2024
Press releases
Amylyx Pharmaceuticals announces completion of enrollment in HELIOS, a Phase 2 Study of AMX0035 for the Treatment of Wolfram Syndrome
By admin
9 February 2024
Press releases
MEF2C Foundation & MUSC launch program to develop MEF2C therapeutics
By admin
9 February 2024
Press releases
National Tay-Sachs & Allied Diseases Association hosts first of its kind drug development meeting for GM2
By admin
2 February 2024
Press releases
Get Ready to #ShowYourStripes for Rare Disease Day 2024 29th February: the rarest day of the year!
By admin
1 February 2024
Press releases
CureDuchenne announces educational events for families and caregivers of individuals with Duchenne or Becker muscular dystrophy
By admin
31 January 2024
Press releases
Sickle Cell Disease Association of America Inc. appoints two to board
By admin
29 January 2024
Press releases
American Kidney Fund announces April 30 as the first annual APOL1-mediated kidney disease (AMKD) awareness day
By admin
26 January 2024
Press releases
REGISTER NOW for M4RD’s ANNUAL SYMPOSIUM
By admin
23 January 2024
1
2
3
…
11
Next »
Skip to content
Open toolbar
Accessibility Tools
Accessibility Tools
Increase Text
Increase Text
Decrease Text
Decrease Text
Grayscale
Grayscale
High Contrast
High Contrast
Negative Contrast
Negative Contrast
Light Background
Light Background
Links Underline
Links Underline
Readable Font
Readable Font
Reset
Reset